For Mark Legg

posted in: Fundraising | 0

For Mark Legg: A truly inspirational and brave young man with Noonan’s syndrome who last week lost his fight with increasing complicated health issues. Please help us to now raise money in his honour so the charity for which his … Continued

What is gene therapy?

posted in: Research | 0

Around 80% of rare diseases have a genetic cause. Many of these diseases have no good treatment options, but gene therapy might help. So what is gene therapy, and how does it work? Raremark have produced an article we think … Continued